Clinical Trials for Mitochondrial Disease

MitoCanada is committed to curating an active list of clinical trials important to patients and mitochondrial disease research.

Dichloroacetate (DCA) PDC Deficiency Study, USA

Phase 3 trial of DCA in young children with PDC

Enrolment: Recruiting now

Study Site: Multi-USA site; Canadian recruits welcome

Update: Press Release – GeneDx is collaborating with Saol Therapeutics to find patients with PDCD

Dichloroacetate (DCA) PDC Deficiency Study, USA

Phase 3 trial of DCA in young children with PDC

Enrolment: Recruiting now

Study Site: Multi-USA site; Canadian recruits welcome

Update: Press Release – GeneDx is collaborating with Saol Therapeutics to find patients with PDCD